Doctors have successfully dealt with a child’s first treatment for genes

A team of doctors and scientists has successfully dealt with a rare genetic condition with the first treatment for genes. The results of the pioneering treatment were in New England Magazine for MedicineWith accompanying By a doctor who had previously supervised the efforts to organize genes in the Food and Drug Administration (FDA).

The patient on this date KJ, a CPS1 deficiency child, was about 50 percent of the death rate during the first week. Patients who keep survival can experience severe brain diseases, mental and developmental delay, and potential liver transplants. The sponsorship team has developed a dedicated treatment for genes on the basis of CRISPR, a technique for modifying the human DNA.

KJ’s successful genes combined from medical research funded by the former federal government, including the discovery of CRISPR and the human genome sequence that allowed to determine the mutation.

This approach is likely to be used to release future genes to help patients with other genetic disorders, such as sickle cell disease, cystic fibrosis, Huntington disease and muscularism. A pair of Krisper -based drugs has already received As for the treatment of sickle cell disease, but there is still a lot to be explore In this field.